Posts tagged with orphan-drug-act

Happy birthday Elaprase!

Posted Wednesday July 24, 2013 by Melissa

Today is the 7th anniversary of the FDA approval of Elaprase (idursulfase)...

Today is the 7th anniversary of the FDA approval of Elaprase (idursulfase) as the first treatment for Hunter Syndrome. On July 24, 2006, the FDA approved Elaprase. It provided HOPE....

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Why I Fear the Bubble, Part 1: The Pricing of #RareDisease Drugs

Posted Saturday January 05, 2013 by Melissa

NPS Pharmaceuticals just this week priced their drug for short bowel syndrome,...

NPS Pharmaceuticals just this week priced their drug for short bowel syndrome, Gattex, at an annual cost of $295,000 per patient. This price may not raise too many eyebrows among...

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