Posts tagged with advocacy-2

What proof does the FDA want in a degenerative disease?

Posted Thursday January 16, 2014 by Melissa

Here is an example in Duchenne MD of why I spent last...

Here is an example in Duchenne MD of why I spent last week at the FDA. In a degenerative disease, if a drug can maintain abilities, why do children have...

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Sometimes we run, when we don’t want to

Posted Saturday April 28, 2012 by Melissa

Today I have a race. A race I didn’t train for. And...

Today I have a race. A race I didn’t train for. And I’m running alone. Will I finish? I hope so. Will I collapse? I hope not. Will I do...

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Advocacy Series: Advocacy in 4 Steps

Posted Monday October 24, 2011 by Melissa

I recently spoke at an MPS family meeting about advocacy in different...

I recently spoke at an MPS family meeting about advocacy in different contexts and was asked by several families to compile the presentation and slides and share them. Since the...

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Advocacy